Pyrrolo[1,2-a]quinoxalines: Insulin Mimetics that Exhibit Potent and Selective Inhibition against Protein Tyrosine Phosphatase 1B.


Journal

ChemMedChem
ISSN: 1860-7187
Titre abrégé: ChemMedChem
Pays: Germany
ID NLM: 101259013

Informations de publication

Date de publication:
05 10 2020
Historique:
received: 20 06 2020
revised: 29 07 2020
pubmed: 11 9 2020
medline: 31 7 2021
entrez: 10 9 2020
Statut: ppublish

Résumé

PTP1B dephosphorylates insulin receptor and substrates to modulate glucose metabolism. This enzyme is a validated therapeutic target for type 2 diabetes, but no current drug candidates have completed clinical trials. Pyrrolo[1,2-a]quinoxalines substituted at positions C1-C4 and/or C7-C8 were found to be nontoxic to cells and good inhibitors in the low- to sub-micromolar range, with the 4-benzyl derivative being the most potent inhibitor (0.24 μm). Some analogues bearing chlorine atoms at C7 and/or C8 kept potency and showed good selectivity compared to TCPTP (selectivity index >40). The most potent inhibitors behaved as insulin mimetics by increasing glucose uptake. The 4-benzyl derivative inhibited insulin receptor substrate 1 and AKT phosphorylation. Molecular docking and molecular dynamics simulations supported a putative binding mode for these compounds to the allosteric α3/α6/α7 pocket, but inconsistent results in enzyme inhibition kinetics were obtained due to the high tendency of these inhibitors to form stable aggregates. Computational calculations supported the druggability of inhibitors.

Identifiants

pubmed: 32909701
doi: 10.1002/cmdc.202000446
doi:

Substances chimiques

Enzyme Inhibitors 0
Insulin 0
Pyrroles 0
Quinoxalines 0
pyrrolo(1,2-a)quinoxaline 0
PTPN1 protein, human EC 3.1.3.48
Protein Tyrosine Phosphatase, Non-Receptor Type 1 EC 3.1.3.48
Glucose IY9XDZ35W2

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1788-1801

Informations de copyright

© 2020 Wiley-VCH GmbH.

Références

B. J. Goldstein, A. Bittner-Kowalczyk, M. F. White, M. Harbeck, J. Biol. Chem. 2000, 275, 4283-4289.
S. Dadke, J. Kusari, J. Chernoff, J. Biol. Chem. 2000, 275, 23642-23647.
M. Delibegovic, D. Zimmer, C. Kauffman, K. Rak, E. G. Hong, Y. R. Cho, J. K. Kim, B. B. Kahn, B. G. Neel, K. K. Bence, Diabetes 2009, 58, 590-599.
L. D. Klaman, O. Boss, O. D. Peroni, J. K. Kim, J. L. Martino, J. M. Zabolotny, N. Moghal, M. Lubkin, Y. B. Kim, A. H. Sharpe, A. Stricker-Krongrad, G. I. Shulman, B. G. Neel, B. B. Kahn, Mol. Cell. Biol. 2000, 20, 5479-5489.
M. Elchebly, P. Payette, E. Michaliszyn, W. Cromlish, S. Collins, A. L. Loy, D. Normandin, A. Cheng, J. Himms-Hagen, C. C. Chan, C. Ramachandran, M. J. Gresser, M. L. Tremblay, B. P. Kennedy, Science 1999, 283, 1544-1548.
C. M. Rondinone, J. M. Trevillyan, J. Clampit, R. J. Gum, C. Berg, P. Kroeger, L. Frost, B. A. Zinker, R. Reilly, R. Ulrich, M. Butler, B. P. Monia, M. R. Jirousek, J. F. Waring, Diabetes 2002, 51, 2405-2411.
B. A. Zinker, C. M. Rondinone, J. M. Trevillyan, R. J. Gum, J. E. Clampit, J. F. Waring, N. Xie, D. Wilcox, P. Jacobson, L. Frost, P. E. Kroeger, R. M. Reilly, S. Koterski, T. J. Opgenorth, R. G. Ulrich, S. Crosby, M. Butler, S. F. Murray, R. A. McKay, S. Bhanot, B. P. Monia, M. R. Jirousek, Proc. Natl. Acad. Sci. USA 2002, 99, 11357-11362.
Trodusquemine (MSI-1436) completed phase I for obesity and T2DM and currently is suspended at phase I for breast cancer trials (www.clinicaltrials.gov).
Z. Y. Zhang, S. Y. Lee, Expert Opin. Invest. Drugs, 2003, 12, 223-33.
K. A. Lantz, S. G. Hart, S. L. Planey, M. F. Roitman, I. A. Ruiz-White, H. R. Wolfe, M. P. McLane, Obesity, 2010, 18, 1516-1523.
S. Fukuda, T. Ohta, S. Sakata, H. Morinaga, M. Ito, Y. Nakagawa, M. Tanaka, M. Matsushita, Diabetes Obes. Metab. 2010, 12, 299-306.
E. J. Moran, S. Sarshar, J. F. Cargill, M. M. Shahbaz, A. Lio, A. M. M. Mjalli, R. W. Armstrong, J. Am. Chem. Soc. 1995, 117, 10787-10788.
L.-J. Wang, B. Jiang, N. Wu, S.-Y. Wang, D.-Y. Shi, RSC Adv. 2015, 5, 48822-48834.
A. P. Combs, J. Med. Chem. 2010, 53, 2333-2344.
S. De Munter, M. Kohn, M. Bollen, ACS Chem. Biol. 2013, 8, 36-45.
W. Peti, R. Page, Bioorg. Med. Chem. 2015, 23, 2781-2785.
M. A. Ghattas, N. Raslan, A. Sadeq, M. Al Sorkhy, N. Atatreh, Drug Des. Dev. Ther. 2016, 10, 3197-3209.
D. Barford, A. J. Flint, N. K. Tonks, Science 1994, 263, 1397-1404.
A. Salmeen, J. N. Andersen, M. P. Myers, N. K. Tonks, D. Barford, Mol. Cell 2000, 6, 1401-1412.
Y. A. Puius, Y. Zhao, M. Sullivan, D. S. Lawrence, S. C. Almo, Z.-Y. Zhang, Proc. Natl. Acad. Sci. USA 1997, 94, 13420-13425.
P. J. Ala, L. Gonneville, M. Hillman, M. Becker-Pasha, E. W. Yue, B. Douty, B. Wayland, P. Polam, M. L. Crawley, E. McLaughlin, R. B. Sparks, B. Glass, A. Takvorian, A. P. Combs, T. C. Burn, G. F. Hollis, R. Wynn, J. Biol. Chem. 2006, 281, 38013-38021.
C. Wiesmann, K. J. Barr, J. Kung, J. Zhu, D. A. Erlanson, W. Shen, B. J. Fahr, M. Zhong, L. Taylor, M. Randal, R. S. McDowell, S. K. Hansen, Nat. Struct. Mol. Biol. 2004, 11, 730-737.
N. Krishnan, D. Koveal, D. H. Miller, B. Xue, S. D. Akshinthala, J. Kragelj, M. R. Jensen, C.-M. Gauss, R. Page, M. Blackledge, S. K. Muthuswamy, W. Peti, N. K. Tonks, Nat. Chem. Biol. 2014, 10, 558-566.
A. Huang, A. Ma, C. Mini-Rev. Med. Chem. 2013, 13, 607-616.
G. W. H. Cheeseman, B. Tuck, J. Chem. Soc. 1966, 852-855.
M. L. Heffernan, G. M. Irvine, Aust. J. Chem. 1976, 837-845.
J. Montalibet, K. I. Skorey, B. P. Kenedy, Methods 2005, 23, 2-8.
J. García-Marín, J. Biomol. Struct. Dyn. 2020. DOI: 10.1080/07391102.2020.1790421.
R. A. Walsh, PeerJ 2018, 6, e6082.
R. A. Walsh, Anal. Biochem. 2019, 572, 58-62.
J. J. Irwin, D. Duan, H. Torosyan, A. K. Doak, K. T. Ziebart, T. Sterling, G. Tumanian, B. K. Shoichet, J. Med. Chem. 2015, 58, 7076-7087.
S. L. McGovern, E. Caselli, N. Grigorieff, B. K. Shoichet, J. Med. Chem. 2002, 45, 1712-1722.
S. Boulton, R. Selvaratnam, R. Ahmed, K. Van, X. Cheng, G. Melacini, J. Med. Chem. 2019, 62, 5063-5079.
D. Duan, H. Torosyan, D. Elnatan, C. K. McLaughlin, J. Logie, M. S. Shoichet, D. A. Agard, B. K. Shoichet, ACS Chem. Biol. 2017, 12, 282-290.
H. Torosyan, B. K. Shoichet, J. Med. Chem. 2019, 62, 9593-9599.
A. N. Ganesh, E. N. Donders, B. K. Shoichet, M. S. Shoichet, Nano Today, 2018, 19, 188-200.
P. Lewi, E. Arnold, K. Andries, H. Bohets, H. Borghys, A. Clark, F. Daeyaert, K. Das, M. P. de Bethune, M. de Jonge, J. Heeres, L. Koymans, J. Leempoels, J. Peeters, P. Timmerman, W. Van den Broeck, F. Vanhoutte, G. Van't Klooster, M. Vinkers, Y. Volovik, P. A. Janssen, Drugs R&D, 2004, 5, 245-257.
S. R. LaPlante, R. Carson, J. Gillard, N. Aubry, R. Coulombe, S. Bordeleau, P. Bonneau, M. Little, J. O'Meara, P. L. Beaulieu, J. Med. Chem. 2013, 56, 5142-5150.
J. M. Lopez-Nicolas, M. Perez-Gilabert, F. Garcia-Carmona, J. Agric. Food Chem. 2009, 57, 4630-4635.
M. F. Sassano, A. K. Doak, B. L. Roth, B. K. Shoichet, J. Med. Chem. 2013, 56, 2406-2414.
D. Duan, A. K. Doak, L. Nedyalkova, B. K. Shoichet, ACS Chem. Biol. 2015, 10, 978-988.
H. M. Berman, J. Westbrook, Z. Feng, G. Gilliland, T. N. Bhat, H. Weissig, I. N. Shindyalov, P. E. Bourne, Nucleic Acids Res. 2000, 28, 235-242.
A. J. Barr, Future Med. Chem. 2010, 2, 1563-1576.
FlexX version 4.0; BioSolveIT GmbH, Sankt Augustin, Germany, 2019, www.biosolveit.de/FlexX.
S. Li, J. Zhang, S. Lu, W. Huang, L. Geng, Q. Shen, J. Zhang, PLoS One 2014, 9, e97668/1-e97668/10.
L. Bordoli, F. Kiefer, K. Arnold, P. L. Benkert, J. Battey, T. Schwede, Nat. Protoc. 2009, 4, 1-13.
W. Cui, Y.-H. Cheng, L.-L. Geng, D.-S. Liang, T.-J. Hou, M.-J. Ji, J. Chem. Inf. Model. 2013, 53, 1157-1167.
A. Daina, O. Michielin, V. Zoete, Sci. Rep. 2017, 7, 42717/1-42717/13.
J. Baell, M. A. Walters, Nature 2014, 513, 481-483.
A. Daina, O. Michielin, V. Zoete, J. Chem. Inf. Model. 2014, 54, 3284-3301.
C. Abad-Zapatero, J. T. Metz, Drug Discovery Today 2005, 10, 464-469.
H. Yuan, Y. Hu, Y. Zhu, Y. Zhang, C. Luo, Z. Li, T. Wen, W. Zhuang, J. Zou, L. Hong, X. Zhang, I. Hisatome, T. Yamamoto, J. Cheng, Mol. Cell. Endocrinol. 2017, 443, 138-145.
F. Angius, A. Floris, Toxicol. in Vitro 2015, 29, 314-319.
H. Yoshitomi, R. Tsuru, L. Li, J. Zhou, M. Kudo, T. Liu, M. Gao, PLoS One, 2017, 8, e0183988/1- e0183988/13.
M. Hatem-Vaquero, M. Griera, A. García-Jerez, A. Luengo, J. Álvarez, J. A. Rubio, L. Calleros, D. Rodríguez-Puyol, M. Rodríguez-Puyol, S. De Frutos, J. Endocrinol. 2017, 234, 115-128.
N. Guex, M. C. Peitsch, T. Schwede, Electrophoresis, 2009, 30, S162-S173.
P. Benkert, M. Kuenzli, T. Schwede, Nucleic Acids Res. 2009, 37, W510-W514.
M. J. Frisch, G. W. Trucks, H. B. Schlegel, G. E. Scuseria, M. A. Robb, J. R. Cheeseman, J. A. Montgomery, Jr., T. Vreven, K. N. Kudin, J. C. Burant, J. M. Millam, S. S. Iyengar, J. Tomasi et al., Gaussian 03, Revision C.02, Gaussian, Inc.: Wallingford CT, 2004.
M. Purwn, J. Hernandez-Toribio, C. Coderch, R. Panchuk, N. Skorokhyd, K. Filipiak, B. de Pascual-Teresa, A. Ramos, RSC Adv. 2016, 6, 66595-66608.
T. Darden, D. York, L. Pedersen, J. Chem. Phys. 1993, 92, 10089-10092.
M. A. Lill, Biochemistry, 2011, 50, 6157-6169.
D. R. Roe, T. E. Cheatham, J. Chem. Theory Comput. 2013, 9, 3084-3095.
J. Klett, A. Nunez-Salgado, H. G. Dos Santos, A. Cortes-Cabrera, A. Perona, R. Gil-Redondo, D. Abia, F. Gago, A. Morreale, J. Chem. Theory Comput. 2012, 8, 3395-3408.
C. Selvaraj, S. K. Triphati, K. K. Reddy, S. K. Singh, Curr. Trends Biotechnol. Pharm. 2011, 5, 1104-1109.

Auteurs

Javier García-Marín (J)

Departamento de Química Orgánica y Química Inorgánica, Universidad de Alcalá, 28805, Alcalá de Henares, Spain.
Instituto Ramón y Cajal de Investigación Sanitaria (IRYCIS), Ctra. Colmenar Viejo, km. 9100, 28034, Madrid, Spain.
Instituto de Investigación Química Andrés M. del Río, Facultad de Farmacia, Universidad de Alcalá, 28805, Alcalá de Henares, Spain.

Mercedes Griera (M)

Instituto Ramón y Cajal de Investigación Sanitaria (IRYCIS), Ctra. Colmenar Viejo, km. 9100, 28034, Madrid, Spain.
Departamento de Biología de Sistemas, Universidad de Alcalá, 28805, Alcalá de Henares, Spain.

Patricia Sánchez-Alonso (P)

Departamento de Química Orgánica y Química Inorgánica, Universidad de Alcalá, 28805, Alcalá de Henares, Spain.

Bruno Di Geronimo (B)

Departamento de Química y Bioquímica, Facultad de Farmacia, Universidad San Pablo CEU, 28925, Alcorcón, Spain.

Francisco Mendicuti (F)

Departamento de Química Analítica, Química Física e Ingeniería Química, Universidad de Alcalá, 28805, Alcalá de Henares, Spain.
Instituto de Investigación Química Andrés M. del Río, Facultad de Farmacia, Universidad de Alcalá, 28805, Alcalá de Henares, Spain.

Manuel Rodríguez-Puyol (M)

Instituto Ramón y Cajal de Investigación Sanitaria (IRYCIS), Ctra. Colmenar Viejo, km. 9100, 28034, Madrid, Spain.
Departamento de Biología de Sistemas, Universidad de Alcalá, 28805, Alcalá de Henares, Spain.

Ramón Alajarín (R)

Departamento de Química Orgánica y Química Inorgánica, Universidad de Alcalá, 28805, Alcalá de Henares, Spain.
Instituto Ramón y Cajal de Investigación Sanitaria (IRYCIS), Ctra. Colmenar Viejo, km. 9100, 28034, Madrid, Spain.
Instituto de Investigación Química Andrés M. del Río, Facultad de Farmacia, Universidad de Alcalá, 28805, Alcalá de Henares, Spain.

Beatriz de Pascual-Teresa (B)

Departamento de Química y Bioquímica, Facultad de Farmacia, Universidad San Pablo CEU, 28925, Alcorcón, Spain.

Juan J Vaquero (JJ)

Departamento de Química Orgánica y Química Inorgánica, Universidad de Alcalá, 28805, Alcalá de Henares, Spain.
Instituto Ramón y Cajal de Investigación Sanitaria (IRYCIS), Ctra. Colmenar Viejo, km. 9100, 28034, Madrid, Spain.
Instituto de Investigación Química Andrés M. del Río, Facultad de Farmacia, Universidad de Alcalá, 28805, Alcalá de Henares, Spain.

Diego Rodríguez-Puyol (D)

Instituto Ramón y Cajal de Investigación Sanitaria (IRYCIS), Ctra. Colmenar Viejo, km. 9100, 28034, Madrid, Spain.
Departamento de Biología de Sistemas, Universidad de Alcalá, 28805, Alcalá de Henares, Spain.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH