Mutation in IL36RN impairs the processing and regulatory function of the interleukin-36-receptor antagonist and is associated with DITRA syndrome.


Journal

Experimental dermatology
ISSN: 1600-0625
Titre abrégé: Exp Dermatol
Pays: Denmark
ID NLM: 9301549

Informations de publication

Date de publication:
10 2019
Historique:
accepted: 04 05 2017
pubmed: 13 6 2017
medline: 12 9 2020
entrez: 13 6 2017
Statut: ppublish

Résumé

The identification of loss-of-function mutations of the IL36RN gene encoding the interleukin-36 receptor antagonist (IL-36Ra) in generalized pustular psoriasis (GPP) emphasized the key role of this pathway in skin innate immunity and systemic inflammation. It has been previously shown in vitro that removal of the N-terminal amino acid IL36Ra (M1) is critical to its biological activity, but the in vivo contribution of this processing remains unknown. We report herein a new homozygous (c4G>T, pV2F) missense IL36RN mutation segregating in a family with three GPP-affected patients. The V2F mutation does not alter IL-36Ra protein expression but was devoid of any antagonist activity. Mass spectrometry showed that the V2F IL-36Ra mutant retains its first N-terminal methionine. These results provide the first in vivo demonstration that removal of N-terminal methionine of native IL-36Ra is a mandatory step to reach optimal antagonist activity and to prevent sustained skin and systemic inflammation in humans.

Identifiants

pubmed: 28603914
doi: 10.1111/exd.13387
doi:

Substances chimiques

IL36RN protein, human 0
Interleukins 0
C-Reactive Protein 9007-41-4

Types de publication

Case Reports Letter Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1114-1117

Subventions

Organisme : SOCIETE FRANCAISE DE DERMATOLOGIE
Pays : International
Organisme : PHRC
Pays : International
Organisme : Amgen Inc.
Pays : International
Organisme : Pfizer
Pays : International

Informations de copyright

© 2017 John Wiley & Sons A/S. Published by John Wiley & Sons Ltd.

Auteurs

Elodie Bal (E)

Sorbonne Paris Cité, IMAGINE Institute, Necker Hospital, Enfants-Malades, UMR 1163, Paris-Descartes University, Paris, France.

Ai Ching Lim (AC)

Inflammation Research and Therapeutic Discovery, Amgen Inc., Seattle, WA, USA.

Min Shen (M)

Inflammation Research and Therapeutic Discovery, Amgen Inc., Seattle, WA, USA.

Jason Douangpanya (J)

Inflammation Research and Therapeutic Discovery, Amgen Inc., Seattle, WA, USA.

Marine Madrange (M)

Sorbonne Paris Cité, IMAGINE Institute, Necker Hospital, Enfants-Malades, UMR 1163, Paris-Descartes University, Paris, France.

Rihab Gazah (R)

Sorbonne Paris Cité, IMAGINE Institute, Necker Hospital, Enfants-Malades, UMR 1163, Paris-Descartes University, Paris, France.

Marie Tauber (M)

Sorbonne Paris Cité, IMAGINE Institute, Necker Hospital, Enfants-Malades, UMR 1163, Paris-Descartes University, Paris, France.

Walid Beghdadi (W)

Clinical Research Unit, APHP Saint-Louis Hospital, Paris, France.

Jean Laurent Casanova (JL)

Rockefeller Branch, St. Giles Laboratory of Human Genetics of Infectious Diseases, The Rockefeller University, New York, NY, USA.
Necker Branch, Laboratory of Human Genetics of Infectious Diseases, Sorbonne Paris Cité, IMAGINE Institute, Necker Hospital, Enfants-Malades, UMR 1163, Paris-Descartes University, Paris, France.
Pediatric Hematology-Immunology-Rheumatology Unit, AP-HP, Necker Enfants Malades Hospital, Paris, France.

Emmanuelle Bourrat (E)

Sorbonne Paris Cité, Paris Diderot University, Paris, France.
Department of Pediatrics, APHP Robert Debré Hospital, Paris, France.

Hervé Bachelez (H)

Sorbonne Paris Cité, IMAGINE Institute, Necker Hospital, Enfants-Malades, UMR 1163, Paris-Descartes University, Paris, France.
Sorbonne Paris Cité, Paris Diderot University, Paris, France.
Department of Dermatology, APHP, Saint-Louis Hospital, Paris, France.

Jennifer E Towne (JE)

Inflammation Research and Therapeutic Discovery, Amgen Inc., Seattle, WA, USA.
Moved to Janssen Research & Development LLC, San Diego, CA, USA.

Asma Smahi (A)

Sorbonne Paris Cité, IMAGINE Institute, Necker Hospital, Enfants-Malades, UMR 1163, Paris-Descartes University, Paris, France.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH