Valentina Ghiaccio

Affiliations

Department of Pediatrics, The Children's Hospital of Philadelphia, Philadelphia, USA.

Publications (7)

2'-O-methoxyethyl splice-switching oligos correct splicing from IVS2-745 β-thalassemia patient cells restoring HbA production and chain rebalance.

Haematologica

Avec: Alisa Dong , Valentina Ghiaccio , Irene Motta , Shuling Guo , Raechel Peralta , Susan M Freier , Andy Watt , Sagar Damle , Yasuhiro Ikawa , Danuta Jarocha , Maxwell Chappell , Coralea Stephanou , Paola Delbini , Connie Chen , Soteroula Christou , Marina Kleanthous , Kim Smith-Whitley , Deepa Manwani , Carla Casu , Osheiza Abdulmalik , Maria Domenica Cappellini , Stefano Rivella , Laura Breda

Mitochondria Biogenesis Modulates Iron-Sulfur Cluster Synthesis to Increase Cellular Iron Uptake.

DNA and cell biology

Avec: Ping La , Joseph H Oved , Valentina Ghiaccio , Stefano Rivella

Curing Hemoglobinopathies: Challenges and Advances of Conventional and New Gene Therapy Approaches.

Mediterranean journal of hematology and infectious diseases

Avec: Irene Motta , Valentina Ghiaccio , Andrea Cosentino , Laura Breda

Lentiviral vector ALS20 yields high hemoglobin levels with low genomic integrations for treatment of beta-globinopathies.

Molecular therapy : the journal of the American Society of Gene Therapy

Avec: Laura Breda , Valentina Ghiaccio , Naoto Tanaka , Danuta Jarocha , Yasuhiro Ikawa , Osheiza Abdulmalik , Alisa Dong , Carla Casu , Tobias D Raabe , Xiaochuan Shan , Gwenn A Danet-Desnoyers , Aoife M Doto , John Everett , Frederic D Bushman , Enrico Radaelli , Charles A Assenmacher , James C Tarrant , Natalie Hoepp , Ryo Kurita , Yukio Nakamura , Virginia Guzikowski , Kim Smith-Whitley , Janet L Kwiatkowski , Stefano Rivella

Protocol for a high titer of BaEV-Rless pseudotyped lentiviral vector: Focus on syncytium formation and detachment.

Journal of virological methods

Avec: Kazuhiro Noguchi , Yasuhiro Ikawa , Mika Takenaka , Yuta Sakai , Toshihiro Fujiki , Rie Kuroda , Maxwell Chappell , Valentina Ghiaccio , Stefano Rivella , Taizo Wada

Gene Therapy for Beta-Hemoglobinopathies: Milestones, New Therapies and Challenges.

Molecular diagnosis & therapy

Avec: Valentina Ghiaccio , Maxwell Chappell , Stefano Rivella , Laura Breda

Use of HSC Targeted LNP to Generate a Mouse Model of Lethal α-Thalassemia and Treatment via Lentiviral Gene Therapy.

Blood

Avec: Maxwell Elliott Chappell , Laura Breda , Lucas Tricoli , Amaliris Guerra , Danuta Jadwiga Jarocha , Carlo Castruccio Castracani , Tyler Ellis Papp , Naoto Tanaka , Nolan Hamilton , Michael Paul Triebwasser , Valentina Ghiaccio , Megan Fedorky , Kandace Gollomp , Veronica Bochenek , Aoife M Roche , John K Everett , Emma J Cook , Frederic D Bushman , Nattiya Teawtrakul , Stavros Glentis , Antonis Kattamis , Barbara L Mui , Ying K Tam , Drew Weissman , Osheiza Abdulmalik , Hamideh Parhiz , Stefano Rivella

Réseau de co-auteurs

Stefano Rivella 6 collaborations

Laura Breda 5 collaborations

Yasuhiro Ikawa 3 collaborations

Maxwell Chappell 3 collaborations

Osheiza Abdulmalik 3 collaborations

Alisa Dong 2 collaborations

Irene Motta 2 collaborations

Danuta Jarocha 2 collaborations

Kim Smith-Whitley 2 collaborations

Carla Casu 2 collaborations

Naoto Tanaka 2 collaborations

Frederic D Bushman 2 collaborations

Shuling Guo 1 collaboration

Raechel Peralta 1 collaboration

Susan M Freier 1 collaboration

Andy Watt 1 collaboration

Sagar Damle 1 collaboration

Coralea Stephanou 1 collaboration

Paola Delbini 1 collaboration

Connie Chen 1 collaboration

Soteroula Christou 1 collaboration

Marina Kleanthous 1 collaboration

Deepa Manwani 1 collaboration

Maria Domenica Cappellini 1 collaboration

Ping La 1 collaboration

Joseph H Oved 1 collaboration

Andrea Cosentino 1 collaboration

Tobias D Raabe 1 collaboration

Xiaochuan Shan 1 collaboration

Gwenn A Danet-Desnoyers 1 collaboration

Aoife M Doto 1 collaboration

John Everett 1 collaboration

Enrico Radaelli 1 collaboration

Charles A Assenmacher 1 collaboration

James C Tarrant 1 collaboration

Natalie Hoepp 1 collaboration

Ryo Kurita 1 collaboration

Yukio Nakamura 1 collaboration

Virginia Guzikowski 1 collaboration

Janet L Kwiatkowski 1 collaboration

Kazuhiro Noguchi 1 collaboration

Mika Takenaka 1 collaboration

Yuta Sakai 1 collaboration

Toshihiro Fujiki 1 collaboration

Rie Kuroda 1 collaboration

Taizo Wada 1 collaboration

Maxwell Elliott Chappell 1 collaboration

Lucas Tricoli 1 collaboration

Amaliris Guerra 1 collaboration

Danuta Jadwiga Jarocha 1 collaboration

Carlo Castruccio Castracani 1 collaboration

Tyler Ellis Papp 1 collaboration

Nolan Hamilton 1 collaboration

Michael Paul Triebwasser 1 collaboration

Megan Fedorky 1 collaboration

Kandace Gollomp 1 collaboration

Veronica Bochenek 1 collaboration

Aoife M Roche 1 collaboration

John K Everett 1 collaboration

Emma J Cook 1 collaboration

Nattiya Teawtrakul 1 collaboration

Stavros Glentis 1 collaboration

Antonis Kattamis 1 collaboration

Barbara L Mui 1 collaboration

Ying K Tam 1 collaboration

Drew Weissman 1 collaboration

Hamideh Parhiz 1 collaboration