Maria Carmina Castiello

Affiliations

San Raffaele Telethon Institute for Gene Therapy SR-Tiget, IRCCS San Raffaele Scientific Institute, Milan, Cagliari, Italy; Institute of Genetic and Biomedical Research Milan Unit, National Research Council, Milan, Cagliari, Italy.

Publications (9)

Efficacy and safety of anti-CD45-saporin as conditioning agent for RAG deficiency.

The Journal of allergy and clinical immunology

Avec: Maria Carmina Castiello , Marita Bosticardo , Nicolò Sacchetti , Enrica Calzoni , Elena Fontana , Yasuhiro Yamazaki , Elena Draghici , Cristina Corsino , Ileana Bortolomai , Lucia Sereni , Hsin-Hui Yu , Paolo Uva , Rahul Palchaudhuri , David T Scadden , Anna Villa , Luigi D Notarangelo

Lentiviral gene therapy corrects platelet phenotype and function in patients with Wiskott-Aldrich syndrome.

The Journal of allergy and clinical immunology

Avec: Lucia Sereni , Maria Carmina Castiello , Dario Di Silvestre , Patrizia Della Valle , Chiara Brombin , Francesca Ferrua , Maria Pia Cicalese , Loris Pozzi , Maddalena Migliavacca , Maria Ester Bernardo , Claudio Pignata , Roula Farah , Lucia Dora Notarangelo , Nufar Marcus , Lorella Cattaneo , Marco Spinelli , Stefania Giannelli , Marita Bosticardo , Koen van Rossem , Armando D'Angelo , Alessandro Aiuti , Pierluigi Mauri , Anna Villa

Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper-IgM syndrome.

EMBO molecular medicine

Avec: Valentina Vavassori , Elisabetta Mercuri , Genni E Marcovecchio , Maria C Castiello , Giulia Schiroli , Luisa Albano , Carrie Margulies , Frank Buquicchio , Elena Fontana , Stefano Beretta , Ivan Merelli , Andrea Cappelleri , Paola Mv Rancoita , Vassilios Lougaris , Alessandro Plebani , Maria Kanariou , Arjan Lankester , Francesca Ferrua , Eugenio Scanziani , Cecilia Cotta-Ramusino , Anna Villa , Luigi Naldini , Pietro Genovese

Innovative Cell-Based Therapies and Conditioning to Cure RAG Deficiency.

Frontiers in immunology

Avec: Anna Villa , Valentina Capo , Maria Carmina Castiello

Thymic Epithelial Cell Alterations and Defective Thymopoiesis Lead to Central and Peripheral Tolerance Perturbation in MHCII Deficiency.

Frontiers in immunology

Avec: Francesca Ferrua , Ileana Bortolomai , Elena Fontana , Dario Di Silvestre , Rosita Rigoni , Genni Enza Marcovecchio , Elena Draghici , Francesca Brambilla , Maria Carmina Castiello , Gloria Delfanti , Despina Moshous , Capucine Picard , Tom Taghon , Victoria Bordon , Ansgar S Schulz , Catharina Schuetz , Silvia Giliani , Annarosa Soresina , Andrew R Gennery , Sara Signa , Blachy J Dávila Saldaña , Ottavia M Delmonte , Luigi D Notarangelo , Chaim M Roifman , Pietro Luigi Poliani , Paolo Uva , Pier Luigi Mauri , Anna Villa , Marita Bosticardo

Partial correction of immunodeficiency by lentiviral vector gene therapy in mouse models carrying

Frontiers in immunology

Avec: Maria Carmina Castiello , Martina Di Verniere , Elena Draghici , Elena Fontana , Sara Penna , Lucia Sereni , Alessandra Zecchillo , Denise Minuta , Paolo Uva , Marco Zahn , Irene Gil-Farina , Andrea Annoni , Silvia Iaia , Lisa M Ott de Bruin , Luigi D Notarangelo , Karin Pike-Overzet , Frank J T Staal , Anna Villa , Valentina Capo

Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency.

Science translational medicine

Avec: Maria Carmina Castiello , Chiara Brandas , Samuele Ferrari , Simona Porcellini , Nicolò Sacchetti , Daniele Canarutto , Elena Draghici , Ivan Merelli , Matteo Barcella , Gabriele Pelosi , Valentina Vavassori , Angelica Varesi , Aurelien Jacob , Serena Scala , Luca Basso Ricci , Marianna Paulis , Dario Strina , Martina Di Verniere , Lucia Sergi Sergi , Marta Serafini , Steven M Holland , Jenna R E Bergerson , Suk See De Ravin , Harry L Malech , Francesca Pala , Marita Bosticardo , Chiara Brombin , Federica Cugnata , Enrica Calzoni , Gay M Crooks , Luigi D Notarangelo , Pietro Genovese , Luigi Naldini , Anna Villa

Choice of template delivery mitigates the genotoxic risk and adverse impact of editing in human hematopoietic stem cells.

Cell stem cell

Avec: Samuele Ferrari , Aurelien Jacob , Daniela Cesana , Marianne Laugel , Stefano Beretta , Angelica Varesi , Giulia Unali , Anastasia Conti , Daniele Canarutto , Luisa Albano , Andrea Calabria , Valentina Vavassori , Carlo Cipriani , Maria Carmina Castiello , Simona Esposito , Chiara Brombin , Federica Cugnata , Oumeya Adjali , Eduard Ayuso , Ivan Merelli , Anna Villa , Raffaella Di Micco , Anna Kajaste-Rudnitski , Eugenio Montini , Magalie Penaud-Budloo , Luigi Naldini

Correcting inborn errors of immunity: From viral mediated gene addition to gene editing.

Seminars in immunology

Avec: Maria Carmina Castiello , Samuele Ferrari , Anna Villa

Réseau de co-auteurs

Anna Villa 9 collaborations

Marita Bosticardo 4 collaborations

Elena Fontana 4 collaborations

Elena Draghici 4 collaborations

Luigi D Notarangelo 4 collaborations

Lucia Sereni 3 collaborations

Paolo Uva 3 collaborations

Chiara Brombin 3 collaborations

Francesca Ferrua 3 collaborations

Valentina Vavassori 3 collaborations

Ivan Merelli 3 collaborations

Luigi Naldini 3 collaborations

Samuele Ferrari 3 collaborations

Nicolò Sacchetti 2 collaborations

Enrica Calzoni 2 collaborations

Ileana Bortolomai 2 collaborations

Dario Di Silvestre 2 collaborations

Luisa Albano 2 collaborations

Stefano Beretta 2 collaborations

Pietro Genovese 2 collaborations

Valentina Capo 2 collaborations

Martina Di Verniere 2 collaborations

Daniele Canarutto 2 collaborations

Angelica Varesi 2 collaborations

Aurelien Jacob 2 collaborations

Federica Cugnata 2 collaborations

Yasuhiro Yamazaki 1 collaboration

Cristina Corsino 1 collaboration

Hsin-Hui Yu 1 collaboration

Rahul Palchaudhuri 1 collaboration

David T Scadden 1 collaboration

Patrizia Della Valle 1 collaboration

Maria Pia Cicalese 1 collaboration

Loris Pozzi 1 collaboration

Maddalena Migliavacca 1 collaboration

Maria Ester Bernardo 1 collaboration

Claudio Pignata 1 collaboration

Roula Farah 1 collaboration

Lucia Dora Notarangelo 1 collaboration

Nufar Marcus 1 collaboration

Lorella Cattaneo 1 collaboration

Marco Spinelli 1 collaboration

Stefania Giannelli 1 collaboration

Koen van Rossem 1 collaboration

Armando D'Angelo 1 collaboration

Alessandro Aiuti 1 collaboration

Pierluigi Mauri 1 collaboration

Elisabetta Mercuri 1 collaboration

Genni E Marcovecchio 1 collaboration

Maria C Castiello 1 collaboration

Giulia Schiroli 1 collaboration

Carrie Margulies 1 collaboration

Frank Buquicchio 1 collaboration

Andrea Cappelleri 1 collaboration

Paola Mv Rancoita 1 collaboration

Vassilios Lougaris 1 collaboration

Alessandro Plebani 1 collaboration

Maria Kanariou 1 collaboration

Arjan Lankester 1 collaboration

Eugenio Scanziani 1 collaboration

Cecilia Cotta-Ramusino 1 collaboration

Rosita Rigoni 1 collaboration

Genni Enza Marcovecchio 1 collaboration

Francesca Brambilla 1 collaboration

Gloria Delfanti 1 collaboration

Despina Moshous 1 collaboration

Capucine Picard 1 collaboration

Tom Taghon 1 collaboration

Victoria Bordon 1 collaboration

Ansgar S Schulz 1 collaboration

Catharina Schuetz 1 collaboration

Silvia Giliani 1 collaboration

Annarosa Soresina 1 collaboration

Andrew R Gennery 1 collaboration

Sara Signa 1 collaboration

Blachy J Dávila Saldaña 1 collaboration

Ottavia M Delmonte 1 collaboration

Chaim M Roifman 1 collaboration

Pietro Luigi Poliani 1 collaboration

Pier Luigi Mauri 1 collaboration

Sara Penna 1 collaboration

Alessandra Zecchillo 1 collaboration

Denise Minuta 1 collaboration

Marco Zahn 1 collaboration

Irene Gil-Farina 1 collaboration

Andrea Annoni 1 collaboration

Silvia Iaia 1 collaboration

Lisa M Ott de Bruin 1 collaboration

Karin Pike-Overzet 1 collaboration

Frank J T Staal 1 collaboration

Chiara Brandas 1 collaboration

Simona Porcellini 1 collaboration

Matteo Barcella 1 collaboration

Gabriele Pelosi 1 collaboration

Serena Scala 1 collaboration

Luca Basso Ricci 1 collaboration

Marianna Paulis 1 collaboration

Dario Strina 1 collaboration

Lucia Sergi Sergi 1 collaboration

Marta Serafini 1 collaboration

Steven M Holland 1 collaboration

Jenna R E Bergerson 1 collaboration

Suk See De Ravin 1 collaboration

Harry L Malech 1 collaboration

Francesca Pala 1 collaboration

Gay M Crooks 1 collaboration

Daniela Cesana 1 collaboration

Marianne Laugel 1 collaboration

Giulia Unali 1 collaboration

Anastasia Conti 1 collaboration

Andrea Calabria 1 collaboration

Carlo Cipriani 1 collaboration

Simona Esposito 1 collaboration

Oumeya Adjali 1 collaboration

Eduard Ayuso 1 collaboration

Raffaella Di Micco 1 collaboration

Anna Kajaste-Rudnitski 1 collaboration

Eugenio Montini 1 collaboration

Magalie Penaud-Budloo 1 collaboration