Adam J Shaywitz

Affiliations

BridgeBio Gene Therapy, Palo Alto, CA, USA.

Publications (4)

Gene-based therapeutics for rare genetic neurodevelopmental psychiatric disorders.

Molecular therapy : the journal of the American Society of Gene Therapy

Avec: Beverly L Davidson , Guangping Gao , Elizabeth Berry-Kravis , Allison M Bradbury , Carsten Bönnemann , Joseph D Buxbaum , Gavin R Corcoran , Steven J Gray , Heather Gray-Edwards , Robin J Kleiman , Adam J Shaywitz , Dan Wang , Huda Y Zoghbi , Terence R Flotte , Sitra Tauscher-Wisniewski , Cynthia J Tifft , Mustafa Sahin , Auteur inconnu

Translational studies of intravenous and intracerebroventricular routes of administration for CNS cellular biodistribution for BMN 250, an enzyme replacement therapy for the treatment of Sanfilippo type B.

Drug delivery and translational research

Avec: Anita Grover , Danielle Crippen-Harmon , Lacey Nave , Jon Vincelette , Jill C M Wait , Andrew C Melton , Roger Lawrence , Jillian R Brown , Katherine A Webster , Bryan K Yip , Brian Baridon , Catherine Vitelli , Sara Rigney , Terri M Christianson , Pascale M N Tiger , Melanie J Lo , John Holtzinger , Adam J Shaywitz , Brett E Crawford , Paul A Fitzpatrick , Jonathan H LeBowitz , Sherry Bullens , Mika Aoyagi-Scharber , Stuart Bunting , Charles A O'Neill , Jason Pinkstaff , Anil Bagri

A phase I/II study on intracerebroventricular tralesinidase alfa in patients with Sanfilippo syndrome type B.

The Journal of clinical investigation

Avec: Nicole Muschol , Anja Koehn , Katharina von Cossel , Ilyas Okur , Fatih Ezgu , Paul Harmatz , Maria J de Castro Lopez , Maria Luz Couce , Shuan-Pei Lin , Spyros Batzios , Maureen Cleary , Martha Solano , Igor Nestrasil , Brian Kaufman , Adam J Shaywitz , Stephen M Maricich , Bernice Kuca , Joseph Kovalchin , Eric Zanelli

Longitudinal Natural History of Pediatric Subjects Affected with Mucopolysaccharidosis IIIB.

The Journal of pediatrics

Avec: Ilyas Okur , Fatih Ezgu , Roberto Giugliani , Nicole Muschol , Anja Koehn , Hernan Amartino , Paul Harmatz , Maria J de Castro Lopez , Maria Luz Couce , Shuan-Pei Lin , Spyros Batzios , Maureen Cleary , Martha Solano , Heidi Peters , Joy Lee , Igor Nestrasil , Adam J Shaywitz , Stephen M Maricich , Bernice Kuca , Joseph Kovalchin , Eric Zanelli

Réseau de co-auteurs

Nicole Muschol 2 collaborations

Anja Koehn 2 collaborations

Ilyas Okur 2 collaborations

Fatih Ezgu 2 collaborations

Paul Harmatz 2 collaborations

Maria J de Castro Lopez 2 collaborations

Maria Luz Couce 2 collaborations

Shuan-Pei Lin 2 collaborations

Spyros Batzios 2 collaborations

Maureen Cleary 2 collaborations

Martha Solano 2 collaborations

Igor Nestrasil 2 collaborations

Stephen M Maricich 2 collaborations

Bernice Kuca 2 collaborations

Joseph Kovalchin 2 collaborations

Eric Zanelli 2 collaborations

Beverly L Davidson 1 collaboration

Guangping Gao 1 collaboration

Elizabeth Berry-Kravis 1 collaboration

Allison M Bradbury 1 collaboration

Carsten Bönnemann 1 collaboration

Joseph D Buxbaum 1 collaboration

Gavin R Corcoran 1 collaboration

Steven J Gray 1 collaboration

Heather Gray-Edwards 1 collaboration

Robin J Kleiman 1 collaboration

Dan Wang 1 collaboration

Huda Y Zoghbi 1 collaboration

Terence R Flotte 1 collaboration

Sitra Tauscher-Wisniewski 1 collaboration

Cynthia J Tifft 1 collaboration

Mustafa Sahin 1 collaboration

None None 1 collaboration

Anita Grover 1 collaboration

Danielle Crippen-Harmon 1 collaboration

Lacey Nave 1 collaboration

Jon Vincelette 1 collaboration

Jill C M Wait 1 collaboration

Andrew C Melton 1 collaboration

Roger Lawrence 1 collaboration

Jillian R Brown 1 collaboration

Katherine A Webster 1 collaboration

Bryan K Yip 1 collaboration

Brian Baridon 1 collaboration

Catherine Vitelli 1 collaboration

Sara Rigney 1 collaboration

Terri M Christianson 1 collaboration

Pascale M N Tiger 1 collaboration

Melanie J Lo 1 collaboration

John Holtzinger 1 collaboration

Brett E Crawford 1 collaboration

Paul A Fitzpatrick 1 collaboration

Jonathan H LeBowitz 1 collaboration

Sherry Bullens 1 collaboration

Mika Aoyagi-Scharber 1 collaboration

Stuart Bunting 1 collaboration

Charles A O'Neill 1 collaboration

Jason Pinkstaff 1 collaboration

Anil Bagri 1 collaboration

Katharina von Cossel 1 collaboration

Brian Kaufman 1 collaboration

Roberto Giugliani 1 collaboration

Hernan Amartino 1 collaboration

Heidi Peters 1 collaboration

Joy Lee 1 collaboration