Systematic elucidation of genetic mechanisms underlying cholesterol uptake.


Journal

bioRxiv : the preprint server for biology
Titre abrégé: bioRxiv
Pays: United States
ID NLM: 101680187

Informations de publication

Date de publication:
10 Jan 2023
Historique:
entrez: 30 1 2023
pubmed: 31 1 2023
medline: 31 1 2023
Statut: epublish

Résumé

Genetic variation contributes greatly to LDL cholesterol (LDL-C) levels and coronary artery disease risk. By combining analysis of rare coding variants from the UK Biobank and genome-scale CRISPR-Cas9 knockout and activation screening, we have substantially improved the identification of genes whose disruption alters serum LDL-C levels. We identify 21 genes in which rare coding variants significantly alter LDL-C levels at least partially through altered LDL-C uptake. We use co-essentiality-based gene module analysis to show that dysfunction of the RAB10 vesicle transport pathway leads to hypercholesterolemia in humans and mice by impairing surface LDL receptor levels. Further, we demonstrate that loss of function of

Identifiants

pubmed: 36711952
doi: 10.1101/2023.01.09.500804
pmc: PMC9881906
pii:
doi:

Types de publication

Preprint

Langues

eng

Subventions

Organisme : Medical Research Council
ID : MC_PC_17228
Pays : United Kingdom
Organisme : NHGRI NIH HHS
ID : R01 HG010372
Pays : United States
Organisme : NHLBI NIH HHS
ID : R01 HL164409
Pays : United States

Commentaires et corrections

Type : UpdateIn

Références

Nature. 2015 Jan 29;517(7536):583-8
pubmed: 25494202
PLoS Genet. 2015 Feb 03;11(2):e1004855
pubmed: 25647241
Nat Biotechnol. 2010 May;28(5):495-501
pubmed: 20436461
Cold Spring Harb Perspect Biol. 2017 Dec 1;9(12):
pubmed: 28246185
J Lipid Res. 2022 Aug;63(8):100248
pubmed: 35753407
Bioinformatics. 2015 Jan 15;31(2):166-9
pubmed: 25260700
Sci Adv. 2016 Dec 16;2(12):e1601470
pubmed: 28028537
Nat Rev Mol Cell Biol. 2020 Apr;21(4):225-245
pubmed: 31848472
Circ Res. 2014 Aug 15;115(5):488-92
pubmed: 24916110
Sci Adv. 2019 Nov 06;5(11):eaax9249
pubmed: 31723604
Cell. 1998 May 29;93(5):731-40
pubmed: 9630218
Am J Hum Genet. 2022 Jan 6;109(1):81-96
pubmed: 34932938
BMC Genomics. 2013;14 Suppl 3:S3
pubmed: 23819870
Development. 1995 Oct;121(10):3279-90
pubmed: 7588062
Cell Rep. 2021 Mar 16;34(11):108873
pubmed: 33730569
PLoS One. 2017 Oct 26;12(10):e0185056
pubmed: 29073143
Cell. 2022 Jul 7;185(14):2559-2575.e28
pubmed: 35688146
Nucleic Acids Res. 2019 May 7;47(8):3846-3861
pubmed: 30864654
Protein Cell. 2015 Jun;6(6):463-467
pubmed: 25860786
PLoS Comput Biol. 2010 Dec 02;6(12):e1001025
pubmed: 21152010
G3 (Bethesda). 2017 Aug 7;7(8):2719-2727
pubmed: 28655737
Nat Rev Genet. 2015 May;16(5):299-311
pubmed: 25854182
N Engl J Med. 2017 Jul 20;377(3):211-221
pubmed: 28538136
Nat Biotechnol. 2016 Feb;34(2):184-191
pubmed: 26780180
Genome Biol. 2016 Jun 06;17(1):122
pubmed: 27268795
N Engl J Med. 2006 Mar 23;354(12):1264-72
pubmed: 16554528
Cell. 2013 Dec 19;155(7):1479-91
pubmed: 24360272
Nature. 2020 May;581(7809):434-443
pubmed: 32461654
Nat Med. 2011 Jun 12;17(7):812-5
pubmed: 21666694
Nature. 1979 Dec 6;282(5739):615-6
pubmed: 233137
Nature. 2020 Jul;583(7818):720-728
pubmed: 32728244
Cold Spring Harb Perspect Biol. 2011 Jul 01;3(7):
pubmed: 21504873
Nat Commun. 2021 Aug 25;12(1):5111
pubmed: 34433825
Nucleic Acids Res. 2020 Jan 8;48(D1):D835-D844
pubmed: 31777943
Arterioscler Thromb Vasc Biol. 2011 Feb;31(2):328-36
pubmed: 21071704
Cell. 2019 Nov 27;179(6):1276-1288.e14
pubmed: 31778654
Nat Methods. 2012 Mar 18;9(5):471-2
pubmed: 22426491
Glob Heart. 2013 Mar;8(1):25-33
pubmed: 25690261
N Engl J Med. 2012 Mar 22;366(12):1154-5
pubmed: 22435375
J Cell Physiol. 2018 Sep;233(9):6483-6494
pubmed: 29377137
Nature. 2021 Nov;599(7886):628-634
pubmed: 34662886
Cell. 2019 Mar 21;177(1):132-145
pubmed: 30901535
Mol Syst Biol. 2018 Dec 20;14(12):e8594
pubmed: 30573688
PLoS Genet. 2021 Jan 29;17(1):e1009285
pubmed: 33513160
Nat Genet. 2000 May;25(1):25-9
pubmed: 10802651
Genome Med. 2020 Dec 2;12(1):103
pubmed: 33261662
Cell Rep. 2020 Nov 24;33(8):108426
pubmed: 33238122
Nat Rev Endocrinol. 2018 Aug;14(8):452-463
pubmed: 29904174
Nat Genet. 2013 Nov;45(11):1274-1283
pubmed: 24097068
Nat Genet. 2017 Sep;49(9):1392-1397
pubmed: 28714974
Nat Methods. 2020 Mar;17(3):261-272
pubmed: 32015543
Nucleic Acids Res. 2015 Jan;43(Database issue):D1049-56
pubmed: 25428369
Am J Hum Genet. 2022 Aug 4;109(8):1366-1387
pubmed: 35931049
Nat Genet. 2017 Jul;49(7):1113-1119
pubmed: 28530674
Curr Opin Lipidol. 2020 Apr;31(2):49-55
pubmed: 32039990
Cell. 2017 Feb 23;168(5):890-903.e15
pubmed: 28162770
Hepatology. 2019 May;69(5):1931-1945
pubmed: 30584660
N Engl J Med. 2017 Jan 5;376(1):41-51
pubmed: 27959715
Nature. 2018 Nov;563(7733):646-651
pubmed: 30405244
N Engl J Med. 2015 Jun 18;372(25):2387-97
pubmed: 26039521
Nat Commun. 2018 Dec 21;9(1):5416
pubmed: 30575746
Genome Biol. 2014;15(12):554
pubmed: 25476604
Nat Protoc. 2019 Mar;14(3):756-780
pubmed: 30710114
Proc Natl Acad Sci U S A. 2008 Aug 19;105(33):11915-20
pubmed: 18695239
J Inherit Metab Dis. 2014 Jul;37(4):609-17
pubmed: 24831587
Nature. 2021 Dec;600(7890):675-679
pubmed: 34887591
Curr Opin Genet Dev. 2019 Feb;54:12-16
pubmed: 30852338
Nature. 2016 Sep 22;537(7621):508-514
pubmed: 27626380
Nat Protoc. 2017 Apr;12(4):828-863
pubmed: 28333914
Nat Genet. 2012 Dec;44(12):1294-301
pubmed: 23104008
Nucleic Acids Res. 2020 Jan 8;48(D1):D127-D131
pubmed: 31504780
Cell Cycle. 2015;14(4):481-7
pubmed: 25607528
Cell. 2014 Oct 23;159(3):635-46
pubmed: 25307933
Pharmacol Res. 2017 Aug;122:53-65
pubmed: 28559211
Proc Natl Acad Sci U S A. 2005 Oct 25;102(43):15545-50
pubmed: 16199517
Elife. 2016 Sep 23;5:
pubmed: 27661255
Cell Metab. 2022 Mar 1;34(3):473-486.e9
pubmed: 35120589
Lancet. 2016 Nov 5;388(10057):2239-2253
pubmed: 27665230
Nat Methods. 2014 Aug;11(8):783-784
pubmed: 25075903
Heart. 2018 Oct;104(19):1600-1607
pubmed: 29622598
J Clin Invest. 2002 May;109(9):1125-31
pubmed: 11994399
Nucleic Acids Res. 2019 Jan 8;47(D1):D607-D613
pubmed: 30476243
Nat Genet. 2015 Oct;47(10):1121-1130
pubmed: 26343387
Nature. 2018 Oct;562(7726):203-209
pubmed: 30305743
J Mol Biol. 2019 Jan 4;431(1):48-65
pubmed: 29959923
Life Sci Alliance. 2019 Apr 12;2(2):
pubmed: 30979825
Bioinformatics. 2013 Jan 1;29(1):15-21
pubmed: 23104886
Nat Genet. 2021 May;53(5):638-649
pubmed: 33859415
Nat Genet. 2014 Mar;46(3):310-5
pubmed: 24487276
Life Sci Alliance. 2020 Dec 16;4(2):
pubmed: 33328249
Nat Genet. 2022 Mar;54(3):240-250
pubmed: 35177841
Nat Genet. 2021 Jul;53(7):942-948
pubmed: 34183854
Cell. 1993 Jun 18;73(6):1125-35
pubmed: 8513497
Mol Ther. 2011 Apr;19(4):731-40
pubmed: 21304496
Front Cell Dev Biol. 2022 Jan 24;10:826379
pubmed: 35141225
Circ Res. 2018 Jun 8;122(12):1648-1660
pubmed: 29545368
Cell Metab. 2009 Jul;10(1):63-75
pubmed: 19583955
Nat Rev Genet. 2019 Dec;20(12):747-759
pubmed: 31605095
Lancet. 2016 Oct 8;388(10053):1459-1544
pubmed: 27733281
Development. 1999 Feb;126(4):743-57
pubmed: 9895322
Nature. 2021 Sep;597(7877):527-532
pubmed: 34375979
Nucleic Acids Res. 2019 Jan 8;47(D1):D419-D426
pubmed: 30407594
Cell. 2017 Jul 27;170(3):564-576.e16
pubmed: 28753430
Nucleic Acids Res. 2022 Jan 7;50(D1):D988-D995
pubmed: 34791404
Nat Rev Cardiol. 2019 Jan;16(1):9-20
pubmed: 29973710
Nat Genet. 2018 Nov;50(11):1514-1523
pubmed: 30275531
Science. 2009 Jul 3;325(5936):100-4
pubmed: 19520913
Genome Res. 2010 Jan;20(1):110-21
pubmed: 19858363
Front Physiol. 2016 Jul 12;7:270
pubmed: 27462273
Nat Commun. 2016 Nov 21;7:13516
pubmed: 27869117
Proc Natl Acad Sci U S A. 2017 Sep 26;114(39):E8224-E8233
pubmed: 28894007
Cell. 2018 Feb 8;172(4):650-665
pubmed: 29425488
J Biol Chem. 2011 May 13;286(19):16541-5
pubmed: 21454697
Mol Cell. 2017 Jul 20;67(2):348-354.e4
pubmed: 28732207
J Lipid Res. 2022 Jan;63(1):100160
pubmed: 34902367
PLoS Genet. 2013;9(2):e1003338
pubmed: 23468663
Sci Transl Med. 2022 Sep 14;14(662):eabj8670
pubmed: 36103516

Auteurs

Marisa C Hamilton (MC)

Division of Genetics, Department of Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, MA 02115, USA.

James D Fife (JD)

Division of Genetics, Department of Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, MA 02115, USA.

Ersin Akinci (E)

Division of Genetics, Department of Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, MA 02115, USA.

Tian Yu (T)

Division of Genetics, Department of Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, MA 02115, USA.

Benyapa Khowpinitchai (B)

Division of Genetics, Department of Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, MA 02115, USA.

Minsun Cha (M)

Division of Genetics, Department of Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, MA 02115, USA.

Sammy Barkal (S)

Division of Genetics, Department of Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, MA 02115, USA.

Thi Tun Thi (TT)

Precision Medicine Research Programme, Yong Loo Lin School of Medicine, National University of Singapore, Singapore.
Cardiovascular Disease Research Programme, Yong Loo Lin School of Medicine, National University of Singapore, Singapore.
Department of Biochemistry, Yong Loo Lin School of Medicine, National University of Singapore, Singapore.

Grace H T Yeo (GHT)

Department of Electrical Engineering and Computer Science, Massachusetts Institute of Technology, Cambridge, MA 02139, USA.

Juan Pablo Ramos Barroso (JP)

Division of Genetics, Department of Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, MA 02115, USA.

Matthew Jake Francoeur (M)

Division of Genetics, Department of Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, MA 02115, USA.

Minja Velimirovic (M)

Division of Genetics, Department of Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, MA 02115, USA.

David K Gifford (DK)

Department of Electrical Engineering and Computer Science, Massachusetts Institute of Technology, Cambridge, MA 02139, USA.
Department of Biological Engineering, Computer Science and Artificial Intelligence Laboratory, Massachusetts Institute of Technology, Cambridge, MA 02139, USA.

Guillaume Lettre (G)

Montreal Heart Institute, Montréal, Québec, H1T 1C8, Canada.
Faculté de Médecine, Université de Montréal, Montréal, Québec, H3T 1J4, Canada.

Haojie Yu (H)

Precision Medicine Research Programme, Yong Loo Lin School of Medicine, National University of Singapore, Singapore.
Cardiovascular Disease Research Programme, Yong Loo Lin School of Medicine, National University of Singapore, Singapore.
Department of Biochemistry, Yong Loo Lin School of Medicine, National University of Singapore, Singapore.

Christopher A Cassa (CA)

Division of Genetics, Department of Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, MA 02115, USA.

Richard I Sherwood (RI)

Division of Genetics, Department of Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, MA 02115, USA.

Classifications MeSH