Molecular genetic and mitochondrial metabolic analyses confirm the suspected mitochondrial etiology in a pediatric patient with an atypical form of alternating hemiplegia of childhood.

Deep sequencing of mitochondrial genome Genotype-phenotype correlation Mitochondrial bioenergetic capacity Oligogenic inheritance Whole exome sequencing

Journal

Molecular genetics and metabolism reports
ISSN: 2214-4269
Titre abrégé: Mol Genet Metab Rep
Pays: United States
ID NLM: 101624422

Informations de publication

Date de publication:
Sep 2020
Historique:
received: 21 05 2020
accepted: 21 05 2020
entrez: 4 6 2020
pubmed: 4 6 2020
medline: 4 6 2020
Statut: epublish

Résumé

Alternative hemiplegia of childhood (AHC) is a rare neurodevelopmental disorder with an extensive phenotypic variability, resulting in a challenging clinical diagnosis. About 75% of AHC cases are caused by pathogenic variants mapping in the

Identifiants

pubmed: 32489883
doi: 10.1016/j.ymgmr.2020.100609
pii: S2214-4269(20)30055-0
pii: 100609
pmc: PMC7262444
doi:

Types de publication

Journal Article

Langues

eng

Pagination

100609

Informations de copyright

© 2020 The Authors.

Déclaration de conflit d'intérêts

The authors declare that they have no conflict of interest.

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Auteurs

Andrea Gropman (A)

Children's National Medical Center, Division of Neurogenetics and Developmental Pediatrics, Washington, DC 20010, USA.

Martine Uittenbogaard (M)

Department of Anatomy and Regenerative Biology, George Washington University School of Medicine and Health Sciences, Washington, DC 20037, USA.

Christine A Brantner (CA)

GW Nanofabrication and Imaging Center, Office of the Vice-President for Research, George Washington University, Washington, DC 20052, USA.

Yue Wang (Y)

Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX 77030, USA.

Lee-Jun Wong (LJ)

Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX 77030, USA.

Anne Chiaramello (A)

Department of Anatomy and Regenerative Biology, George Washington University School of Medicine and Health Sciences, Washington, DC 20037, USA.

Classifications MeSH