A Matter of Genes: The Hurdles of Gene Therapy for Epilepsy.

Gene therapy Viral vectors

Journal

Epilepsy currents
ISSN: 1535-7597
Titre abrégé: Epilepsy Curr
Pays: United States
ID NLM: 101135954

Informations de publication

Date de publication:
Jan 2019
Historique:
entrez: 7 3 2019
pubmed: 7 3 2019
medline: 7 3 2019
Statut: ppublish

Résumé

Gene therapy has recently advanced to the level of standard of care for several diseases. However, its application to neurological disorders is still in the experimental phase. In this review, we discuss recent advancements in the field that provide optimism on the possibility to have first-in-human studies for gene therapy of some forms of epilepsy in the not so distant future.

Identifiants

pubmed: 30838918
doi: 10.1177/1535759718822846
pmc: PMC6610370
doi:

Types de publication

Journal Article

Langues

eng

Pagination

38-43

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Auteurs

Selene Ingusci (S)

1 Department of Medical Sciences and National Institute of Neuroscience, University of Ferrara, Ferrara, Italy.

Stefano Cattaneo (S)

2 School of Medicine, University Vita-Salute San Raffaele, Milan, Italy.

Gianluca Verlengia (G)

1 Department of Medical Sciences and National Institute of Neuroscience, University of Ferrara, Ferrara, Italy.
2 School of Medicine, University Vita-Salute San Raffaele, Milan, Italy.

Silvia Zucchini (S)

1 Department of Medical Sciences and National Institute of Neuroscience, University of Ferrara, Ferrara, Italy.
3 Technopole of Ferrara, LTTA Laboratory for the Technologies for Advanced Therapies, Ferrara, Italy.

Michele Simonato (M)

1 Department of Medical Sciences and National Institute of Neuroscience, University of Ferrara, Ferrara, Italy.
2 School of Medicine, University Vita-Salute San Raffaele, Milan, Italy.

Classifications MeSH